by Rob Copenhaver | Feb 27, 2019
Correction of Familial Hypercholesterolaemia Development and rescue of human familial hypercholesterolaemia in a xenograft mouse model Bissig-Choisat et. al., 2015 – Study Summary Beatrice Bissig-Choisat, Lili Wang, Xavier Legras, Pradip K. Saha, Leon Chen,...
by Rob Copenhaver | Feb 27, 2019
AAV Gene Repair of HT1 Adeno-Assocciated Virus Gene Repair Corrects a Mouse Model of Hereditary Tyrosinemia In Vivo Paulk et. al., 2010 – Study Summary Nicole K. Paulk, Karsten Wursthorn, Zhongya Wang, Milton J. Finegold, Mark A. Kay, and Markus Grompe...
by Rob Copenhaver | Feb 27, 2019
Ex Vivo Correction of HT1 Curative ex vivo hepatocyte-directed gene editing in a mouse model of hereditary tyrosinemia type 1 VanLith et. al., 2018 – Study Summary Caitlin VanLith, Rebekah Guthman, Clara T. Nicolas, Kari Allen, Zeji Du, Dong Jin Joo, Scott L....
